In July, the FDA issued a complete response letter (CRL) for Replimune's biologics license application for RP1 (vusolimogene ...

1 Green Level High School, Cary, NC, United States 2 National Center for Genome Resources, Santa Fe, NM, United States CRISPR-Cas9 is a gene editing tool used extensively in biological research that ...

A genetic disorder that leads to bleeding episodes and life-threatening infections has a new FDA approved treatment, a regulatory decision that marks two notable firsts — the first gene therapy for ...

The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the first therapy of its kind for the rare disease and making Italy’s Fondazione ...

A NEW study revealed that targeting the alarmin S100A11 could offer a powerful therapeutic strategy for metabolic dysfunction–associated steatohepatitis (MASH), a leading cause of chronic liver ...

State Key Laboratory of Oral Diseases, National Center for Stomatology, National Clinical Research Center for Oral Diseases, West China Hospital of Stomatology, Sichuan University, Chengdu, China ...

Revolutions in gene therapy are rapidly changing the landscape of modern medicine. Revolutions in gene therapy are rapidly changing the landscape of modern medicine, forcing society and science alike ...