At a Food and Drug Administration cell and gene therapy (CGT) roundtable last June, most speakers pushed for the agency to ...
Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...
As we continue our series exploring genetic medicine, both in this story and in Destiny's Child No Longer: Rewriting Genetic Fate, gene therapy stands at a crossroads. On June 16, Sarepta Therapeutics ...
Shares of Sarepta Therapeutics plunged more than 30% on Friday as the future of its approved gene therapy treatment appeared at risk. The Food and Drug Administration will request that the company ...
Gene therapies for DMD offer potential benefits but are not curative and carry risks, necessitating informed patient and caregiver perspectives. Early diagnosis through newborn screening raises ...
Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with sickle ...
A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of addiction from narcotics treatments, a breakthrough which could provide hope for ...
A new treatment might just be hope for many people living with chronic pain. In a recent preclinical study, researchers ...
A retired HGV driver was the first person in the world to take part in a clinical trial to extend the lifespan of blood vessels in the heart, using gene therapy. John MacDonald, 73, suffered a heart ...
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