Credit: Getty Images. Pompe disease is a rare, degenerative muscle disorder caused by mutations in the acid alpha-glucosidase gene, which leads to the abnormal buildup of glycogen. The Food and Drug ...
Clinical activity of avapritinib in ≥ fourth-line (4L+) and PDGFRA Exon 18 gastrointestinal stromal tumors (GIST). This is an ASCO Meeting Abstract from the 2020 Gastrointestinal Cancers Symposium.